Paying for precision: funding approaches for N-of-1 trials of individualized gene targeted therapies
Orphanet J Rare Dis. 2026 May 21. doi: 10.1186/s13023-026-04388-1. Online ahead of print. ABSTRACT Individualized medicine has the potential to be a transformative approach to healthcare that tailors medical treatments to the unique makeup of each patient. This report explores the potential of individualized genetic medicines to meet the pressing need for effective treatments for […]